BBC5 年
Gene-silencing: 'New class' of medicine reverses disease porphyria
The condition, acute intermittent porphyria, also causes paralysis and is fatal in some cases. The novel approach fine-tunes the genetic instructions locked in our DNA. Doctors say they are ...
The Focus on MSN16 天
Real life ‘Dracula disease’ can result in vomiting, hallucinations, and aversion to garlic
Count Dracula might have been an invention of the author Bram Stoker, but there is a real-life disease called acute intermittent porphyria that somewhat mimics the symptoms of horror’s scariest ...
BBC3 年
Gene silencing medicine transforms crippling pain
The drug treats acute intermittent porphyria, which runs in families and can leave people unable to work or have a normal life. Clinical trials have shown severe symptoms were cut by 74% with the ...